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Course Lecture Videos

2021 Course Offering of Training in Neurotherapeutics Discovery and Development for Academic Scientists


Session 1: Target and Pathway Interrogation
James Inglese, PhD, National Center for Advancing Translational Sciences, NIH


Session 2: Biology Basics for Identifying Hits
William Janzen, BS, Epizyme, Inc.


Session 3: Moving from Hit to Lead to Clinical Candidate
James Barrow, PhD, Johns Hopkins School of Medicine


Session 4: Antibody-Based Therapies
Gai Ayalon, PhD


Session 6: Intellectual Property
Jeffrey W. Childers, PhD


​Session 7: Alternative Approaches to Lead Generation
Sam J. Enna, PhD, The University of Kansas


Session 8: ADME
Kennan Marsh, PhD, AbbVie


Invited Guest Speaker: The Story of Risdiplam/Everysdi 
Alexander Stephan, PhD, Roche Pharma Research


Session 10: Rigor in Translational Drug Discovery and Development
Shai Silberberg, PhD, NIH/NINDS


Session 11: Toxicology
Adaline Smith, PhD, DABT, Ironwood Pharmaceuticals


Session 12: IND Enabling Studies and Preparation of the IND
Edward Spack, PhD, Medared


Session 13: Formulation and Route of Administration
James Cloyd III, PharmD, University of Minnesota


Session 13: Formulation and Route of Administration
Maureen Donovan, PhD, University of Iowa


Session 13: Antisense Oglionucleotides
Gene Liau, PhD, Stoke Therapeutics


Session 14: Clinical Considerations in the Non-Clinical Phase of Drug Discovery and Development
James Vornov, MD, PhD, Johns Hopkins School of Medicine and Medpace


Session 15: Funding Academic Drug Discovery Research
Charles L. Cywin, PhD, NIH/NINDS